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Updated: Jun 6, 2026

In Vivo Modeling of the Morbid Human Genome using Danio rerio
12:31

In Vivo Modeling of the Morbid Human Genome using Danio rerio

Published on: August 24, 2013

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迎接基因疗法时代:使用主要组件回归来对比蒂晶体的客观分期策略

Chenyue Hang1, Ting Zhang2, Zhixuan Chen1

  • 1From the Department of Ophthalmology (C.H., T.Z., Z.C., T.Z., J.S., T.L., X.W., Y.G., S.Y., H.J., J.C., X.S.), Shanghai General Hospital (Shanghai First People's Hospital), Shanghai Jiao Tong University, School of Medicine, Shanghai, China; Shanghai Key Laboratory of Fundus Diseases (C.H., T.Z., Z.C., T.Z., J.S., T.L., X.W., Y.G., S.Y., H.J., J.C., X.S.), Shanghai, China.

American journal of ophthalmology
|May 29, 2025
PubMed
概括

研究人员使用六个关键指标开发了一种新的对比评分和分期系统,用于比埃蒂晶体缩症 (BCD). 这种新的Bietti晶衰竭评分用于严重性评估 (BCD-SA) 及其相关阶段改善了基因治疗的疾病评估.

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Electroporation-Based Genetic Modification of Primary Human Pigment Epithelial Cells Using the Sleeping Beauty Transposon System07:04

Electroporation-Based Genetic Modification of Primary Human Pigment Epithelial Cells Using the Sleeping Beauty Transposon System

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