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庞贝病成年人的酶替代疗法:从试验到真实世界的数据

Nadine A M E van der Beek1, Lianne H Potters1,2, Benedikt Schoser3

  • 1Department of Neurology.

Current opinion in neurology
|June 5, 2025
PubMed
概括

两种新的佩病酶替代疗法 (ERT) 的疗效和安全性与现有治疗方法相美. 新出现的数据表明,这些新型ERT可能会为患者带来更大的益处和更好的结果.

关键词:
葡萄糖酶阿尔法酶的使用阿瓦尔葡萄糖酶阿尔法葡萄糖化酶阿尔法是什么?酶替代疗法是一种酶替代疗法.晚期发病的庞贝病 晚期发病的庞贝病

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