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Updated: Sep 18, 2025

Electroporation-Based Genetic Modification of Primary Human Pigment Epithelial Cells Using the Sleeping Beauty Transposon System
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Electroporation-Based Genetic Modification of Primary Human Pigment Epithelial Cells Using the Sleeping Beauty Transposon System

Published on: February 4, 2021

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[最近在治疗性夜间血红蛋白尿症方面的进展]

Éléonore Kaphan1, Régis Peffault de Latour1

  • 1Service d'hématologie, hôpital Saint-Louis, Paris, France.

La Revue du praticien
|June 23, 2025
PubMed
概括

近期对性夜间血红蛋白尿症 (PNH) 治疗的进展包括C5抑制剂,但一些患者仍然需要输血. 靠近补充抑制剂在PNH的残留血液溶解管理方面表现有前途.

关键词:
血球蛋白尿症,阳性小血球尿症

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