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Yan-Ling Sun1, Miao Li1, Jing-Jing Liu1

  • 1Department of Pediatrics, Beijing Shijitan Hospital, Capital Medical University, Beijing 100038, China.

概括

分子向疗法在进展性儿科低度质瘤 (pLGG) 中表现有前途. 韦穆拉菲尼布在BRAF V600E突变的PLGG中提供快速瘤缩,而特拉美丁尼布则提供持续的益处.