212:APeX-P

Jolanta Bernatoniene1, Mélisande Bourgoin-Heck2, Mauro Cancian3

  • 1Paediatric Immunology and Infectious Disease Department, Bristol Royal Hospital for Children, Bristol, United Kingdom.

概括

口服贝罗特拉斯塔特为幼儿遗传性血管 (HAE) 提供了耐受性良好,有效的长期预防. 这项研究显示,在12岁以下的患者中,HAE发作率显著降低.

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