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Updated: Sep 8, 2025

Subretinal Injection of Gene Therapy Vectors and Stem Cells in the Perinatal Mouse Eye
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"看星星":基因治疗革命

Gareth D Mercer1, Brian G Ballios1, Peter J Kertes2

  • 1Department of Ophthalmology & Vision Sciences, Temerty Faculty of Medicine, University of Toronto, Toronto, ON, Canada.

Advances in experimental medicine and biology
|July 30, 2025
PubMed
概括

基因疗法通过向特定基因缺陷,为遗传性视网膜疾病 (IRD) 提供一种潜在的治疗方法. 像Luxturna这样的批准治疗方法在治疗这些遗传疾病方面取得了重大进展.

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