Lawrence Lustig1

  • 1Howard W. Smith Professor and Chair, Department of Otolaryngology-Head & Neck Surgery, Columbia University Vagelos College of Physicians and Surgeons, USA.

概括

与奥托弗林相关的听力损失的基因治疗显示出有希望的结果,大多数患者的听力得到改善,一些患者达到正常水平. 这些安全有效的治疗方法标志着遗传性聋症治疗的新时代.