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Updated: Sep 13, 2025

Sequence-specific and Selective Recognition of Double-stranded RNAs over Single-stranded RNAs by Chemically Modified Peptide Nucleic Acids
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Published on: September 21, 2017

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可编程的单链循环反义寡核酸,用于多目标基因治疗

Yufan Pan1, Xin Li1, Chenyou Zhu1

  • 1Engineering Research Center of Advanced Rare Earth Materials (Ministry of Education), Department of Chemistry, Tsinghua University, Beijing 100084, China.

JACS Au
|August 1, 2025
PubMed
概括

循环反感性寡核酸 (circASOs) 为基因疗法提供了一种新的方法,增强稳定性并使多个基因同时沉默以提高治疗效果.

关键词:
反感的寡核化物.化学修饰是一种化学修饰.圆形的 DNA 圆形的 DNA基因调节 基因调节 基因调节多目标疗法多目标疗法

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