访,访

Brooke Krivickas1, Erica Scirocco1, Elisa Giacomelli1

  • 1Sean M. Healey & AMG Center for ALS and Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA.

Muscle & nerve
|August 26, 2025
PubMed
概括

扩展获取协议 (EAP) 为肌缩侧面硬化症 (ALS) 患者提供特雷等试验药物. 这项研究发现三糖不会改变ALS的进展或生物标志物,为未来的EAP建立了框架.