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Updated: May 3, 2026

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脊柱肌肉缩的组合疗法:一个系统的审查

Maryam Bemanalizadeh1,2, Leida Heidary3, Mohammad Sedigh Dakkali4

  • 1Child Growth and Development Research Center, Research Institute for Primordial Prevention of Non-Communicable Disease, Isfahan University of Medical Sciences, Isfahan, Iran.

European journal of pediatrics
|August 29, 2025
PubMed
概括

在脊柱肌肉缩 (SMA) 治疗中,使用nusinersen,onasemnogene abeparvovec-xioi和risdiplam的组合疗法具有前景. 虽然在短期内通常是安全的,但长期的疗效和最佳测序需要进一步研究.

关键词:
组合疗法这是一个很好的机会.只有一个人能做到.其他:脊柱肌肉缩

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