通过设计的安全性:扩大脊髓肌肉缩基因治疗的选择
Ewout J N Groen1, Renske I Wadman1
1Department of Neurology and Neurosurgery, University Medical Center Utrecht, Utrecht, the Netherlands.
Molecular therapy. Methods & clinical development
|September 2, 2025
概括
No abstract available in PubMed .
更多相关视频
06:51Systemic Delivery of MicroRNA Using Recombinant Adeno-associated Virus Serotype 9 to Treat Neuromuscular Diseases in Rodents
Published on: August 10, 2018
7.8K
10:57Intramuscular Injections Along the Motor End Plates: A Minimally Invasive Approach to Shuttle Tracers Directly into Motor Neurons
Published on: July 13, 2015
12.8K
相关概念视频
What is Genetic Engineering?
75.4K
Overview
75.4K
Satellite Stem Cells and Muscular Dystrophy
2.0K
Satellite stem cells or myosatellite cells are quiescent stem cells that Alexander Mauro first identified in 1961. These cells are located between the sarcolemma, the plasma membrane of muscle fibers, and the basal lamina, the connective tissue sheath covering it. These mononucleated cells are activated in response to muscle injury, can transform into myoblasts, and may form or repair muscle fibers. Myosatellite cells can provide additional myonuclei for muscle regeneration or return to a...
2.0K
