在快速采用后评估囊性纤维化调节器疗法的长期有效性:双重方法研究

Pedro Miranda Afonso1, Grace C Zhou2,3, Weiji Su3,4

  • 1Erasmus MC, Department of Epidemiology and Biostatistics, Rotterdam, Zuid-Holland, Netherlands; p.mirandaafonso@erasmusmc.nl.

概括

伊瓦卡夫托尔治疗改善了囊性纤维化 (CF) 患者的肺功能. 在人体内和人体间的分析显示出类似的有效性,尽管对年轻人建议谨慎.

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