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Updated: Jan 18, 2026

Author Spotlight: Advancing the Detection of Low-Frequency Mutations in Cancer Tissues
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罕见疾病中的HTA证据:只是罕见还是特别?

Anirban Basu1, Simu K Thomas2, Richard H Chapman3

  • 1The CHOICE Institute, University of Washington, Seattle, WA, USA.

PharmacoEconomics
|September 9, 2025
PubMed
概括

由于数据有限,开发孤儿药物对健康技术评估提出了独特的挑战. 修改方法和多利益相关者合作对于罕见病药物开发和患者公平至关重要.

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