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Updated: Jan 18, 2026

Lentiviral Vector-mediated Gene Therapy of Hepatocytes Ex Vivo for Autologous Transplantation in Swine
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下一代再生疗法对阿尔法-1抗素缺乏症:分子发病因子到临床翻译

Se-Ran Yang1, Hyung-Ryong Kim2

  • 1Department of Thoracic and Cardiovascular Surgery, School of Medicine, Kangwon National University, Chuncheon 24341, Republic of Korea.

International journal of molecular sciences
|September 13, 2025
PubMed
概括

阿尔法-1抗素缺乏症 (AATD) 通过炎症和中性粒细胞功能障碍导致肺损伤. 诱导多能干细胞和基因编辑为研究AATD提供了新的途径,并为这种遗传性疾病开发了治疗方法.

关键词:
在 AATDD 加入在 AEC2 中,AEC2 是 AEC2.慢性慢性肺炎是一种慢性慢性肺炎,COPD是一种慢性肺炎.愤怒的愤怒 愤怒的愤怒这就是 iPSC 的意义.作为一个中性恋者.

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