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Updated: Jan 17, 2026

Subconjunctival Administration of Adeno-associated Virus Vectors in Small Animal Models
06:16

Subconjunctival Administration of Adeno-associated Virus Vectors in Small Animal Models

Published on: March 16, 2022

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更新基因治疗临床试验对眼睛疾病的最新情况

Nicolas Lonfat1, Laura Moreno-Leon1, Claudio Punzo2

  • 1Astellas Pharma Inc., Westborough, Massachusetts, USA.

Human gene therapy
|September 18, 2025
PubMed
概括

基因疗法为遗传性视网膜疾病提供了有前途的新疗法,如视网膜色素炎和黄斑变性. 目前的临床试验显示了基因特异性和基因不可知性方法的潜力,以恢复视力和对抗失明.

关键词:
与年龄相关的黄斑变性.视网膜 视网膜 视网膜 是一个视网膜退化 视网膜退化

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Subretinal Injection of Gene Therapy Vectors and Stem Cells in the Perinatal Mouse Eye05:09

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