在患有B型血友病的儿童中使用延长半衰期因子IX的现实世界

Athina Dettoraki1, Aikaterini Michalopoulou1, Stefanos Saslis1

  • 1Haemophilia Centre, Haemostasis and Thrombosis Unit, "Aghia Sophia" Children's Hospital, 1 Thivon and Papadiamantopoulou Str., 115 27 Athens, Greece.

Life (Basel, Switzerland)
|September 27, 2025
PubMed
概括

延长半衰期 (EHL) 因子IX产品为血友病B (PWHB) 患者提供了改善的预防,减少出血率和因子消耗. 这项现实研究表明,在儿科患者中成功使用EHL,没有抑制剂的发展.

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