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开发一种以AAV为基础的基因疗法,用于弗里德里希缺氧的眼睛表型

Heyu Tang1, Siddhant Gupte1, Emily Xu1

  • 1Division of Cellular and Molecular Therapy, Department of Pediatrics, University of Florida, Gainesville, FL, USA.

Molecular therapy : the journal of the American Society of Gene Therapy
|October 25, 2025
PubMed
概括

弗里德里希·弗里德里希 (Friedreich Friedreich) 是一个德国人.

关键词:
在 AAV AAV AAV 中.弗里德里希的动脉衰竭是弗里德里希的动脉衰竭.腺相关病毒的病毒.体内输送的交付.鼠标模型 鼠标模型鼠标模型眼部基因疗法 眼部基因疗法视网膜的质细胞细胞.

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