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Updated: Jan 9, 2026

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为临床医生解构血友病中的基因疗法

Guy Young1

  • 1Children's Hospital Los Angeles, Cancer and Blood Disease Institute, University of Southern California Keck School of Medicine, Los Angeles, CA.

Hematology. American Society of Hematology. Education Program
|December 5, 2025
PubMed
概括

血友病A和B的基因疗法现在已经可用,提供了新的治疗选择. 本综述解释了基因治疗的基础知识,批准的治疗方法,以及为共享决策的临床实施.

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