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脊柱肌肉缩的治疗演变:来自SMArtCARE注册表的见解

Cornelia Voigt-Müller1, Michelle Pfaffenlehner2,3, Günther Bernert4

  • 1Department of Neuropediatrics and Muscle Disorders, Medical Center - University of Freiburg, Faculty of Medicine, University of Freiburg, D-79106 Freiburg, Germany.

Brain : a journal of neurology
|December 23, 2025
PubMed
概括

对5q脊柱肌肉缩 (SMA) 的现实世界治疗表明,大多数患者继续接受他们的第一个疾病修饰治疗 (DMT). 在SMA患者的治疗切换通常发生在新的DMT批准后,并且与运动功能变化无关.

关键词:
这是DMT DMT.在此期间,SMA SMA SMA改变疾病的治疗方法.脊柱肌肉缩 脊柱肌肉缩 脊柱肌肉缩

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