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药物开发 药物开发

Dominique Taillie1, Diana Cha1, Gina Ferraro1

  • 1Alnylam Pharmaceuticals, Cambridge, MA, USA.

Alzheimer's & dementia : the journal of the Alzheimer's Association
|December 25, 2025
PubMed
概括

用APP降低siRNA的早期干预显著减少了阿尔茨海默病的病理学,并防止了小鼠模型中的行为缺陷. 这种RNAi治疗方法在治疗阿尔茨海默病方面表现有前途.

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