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Updated: Jan 7, 2026

Drug Repurposing Hypothesis Generation Using the "RE:fine Drugs" System
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药物开发 药物开发

Yi-Ge Huang1, Jane Yc Chan1, Rachel Sartaj1

  • 1AviadoBio Ltd., London, United Kingdom.

Alzheimer's & dementia : the journal of the Alzheimer's Association
|December 25, 2025
PubMed
概括

对前性痴呆症 (FTD-GRN) 的AVB-101基因疗法在第一批患者中显示出良好的安全性和耐受性. 早期结果表明,这种治疗对FTD-GRN有希望,目前正在进行更高剂量的试验.

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