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Updated: Jan 7, 2026

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药物开发 药物开发

Tiffini Voss1, Paulette Triglia1, Yan G Ni2

  • 1PassageBio, Philadelphia, PA, USA.

Alzheimer's & dementia : the journal of the Alzheimer's Association
|December 26, 2025
PubMed
概括

PBFT02基因疗法通过增加进激素水平,对前性痴呆症 (FTD) 呈现有前途的效果. 早期的数据表明,FTD-GRN可能成为一次性治疗,支持进一步的临床开发.

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