Hye Jin Lee1, Yunxuan Xie2, Colin F Greineder3

  • 1Department of Pharmaceutical Sciences, University of Michigan, Ann Arbor, MI 48109, USA; College of Pharmacy, Chungbuk National University, Cheongju 28160, Republic of Korea.

PubMed
概括

寡核酸治疗药物为中枢神经系统疾病提供向基因治疗. 工程化,抗体和脂质结合物增强了穿越血脑屏障的传递,提高了神经疾病的治疗疗效.