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Updated: Jan 20, 2026

Continuous Manual Exchange Transfusion for Patients with Sickle Cell Disease: An Efficient Method to Avoid Iron Overload
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Published on: March 14, 2017

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对状细胞疾病的基因疗法

Colleen H Dansereau1

  • 1Clinical and Translational Investigation Program, Boston Children's Hospital, Boston, MA, USA.

Journal of pediatric hematology/oncology nursing
|January 19, 2026
PubMed
概括

基因疗法通过基因修改患者的干细胞,为状细胞疾病 (SCD) 提供了潜在的治疗方法. 早期的临床试验显示,经批准的治疗方法带来了有希望的结果,这突显了护理支持的重要性.

关键词:
基因治疗的基因疗法精准医学是一门精准医学.状细胞疾病是一种状细胞疾病.

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