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Updated: Jan 24, 2026

Development of an Alpha-synuclein Based Rat Model for Parkinson's Disease via Stereotactic Injection of a Recombinant Adeno-associated Viral Vector
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基于病毒载体的基因疗法在临床上:最新情况

Kyung Soo Park1,2, Yong In Cho1, Samir Mitragotri1,2

  • 1John A. Paulson School of Engineering and Applied Sciences Harvard University Cambridge Massachusetts USA.

Bioengineering & translational medicine
|January 23, 2026
PubMed
概括

使用病毒载体的基因疗法,特别是腺相关病毒 (AAV) 载体,正在迅速发展. 最近的FDA批准强调了它们在治疗各种疾病方面的成功,正在进行的研究扩大了它们的应用.

关键词:
腺病毒的病毒.腺相关病毒的病毒.临床翻译 临床翻译临床试验是指临床试验中的临床试验.基因 基因 基因 基因基因治疗的基因疗法疹简单病毒病毒.病毒载体病毒载体

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