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Updated: Jan 24, 2026

Measuring Glucose Uptake in Drosophila Models of TDP-43 Proteinopathy
07:07

Measuring Glucose Uptake in Drosophila Models of TDP-43 Proteinopathy

Published on: August 3, 2021

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双向的snRNA基因疗法在TDP-43蛋白质病变中挽救了STMN2和UNC13A拼接

Trent A Gomberg, Sara Elmsaouri, Hema M Kopalle

    bioRxiv : the preprint server for biology
    |January 23, 2026
    PubMed
    概括

    这项研究介绍了一种新型基因疗法,使用小核RNA (snRNA) 来纠正肌缩侧面硬化 (ALS) 和其他TDP-43蛋白病变中的错误基因拼接,恢复神经元功能.

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    Novel Atomic Force Microscopy Based Biopanning for Isolation of Morphology Specific Reagents against TDP-43 Variants in Amyotrophic Lateral Sclerosis13:31

    Novel Atomic Force Microscopy Based Biopanning for Isolation of Morphology Specific Reagents against TDP-43 Variants in Amyotrophic Lateral Sclerosis

    Published on: February 12, 2015

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