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Updated: Feb 10, 2026

Trabecular Meshwork Response to Pressure Elevation in the Living Human Eye
09:03

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Published on: June 20, 2015

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通过脂质纳米粒子介导的状网状网络的基层编辑在体内拯救了玻璃眼

Balasankara Reddy Kaipa1, Linya Li1, Prakadeeswari Gopalakrishnan1

  • 1Gavin Herbert Eye Institute-Center for Translational Vision Research, Department of Ophthalmology.

JCI insight
|February 9, 2026
PubMed
概括

一个新的脂质纳米粒子 (LNP) 平台为眼细胞提供基因编辑工具,有效地治疗由MYOC突变引起的玻璃眼病. 这种非病毒方法显示,与传统的病毒载体相比,它具有更高的安全性和效率,用于绿眼病基因治疗.

关键词:
基因治疗是一种基因疗法.遗传性疾病是一种遗传性疾病.遗传学 是一个遗传学.眼科医生 眼科 眼科蛋白质的错误折叠 蛋白质的错误折叠

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