磁力共振成像 (MRI) 结果在脊髓小脑动症1和3的预防性和早期试验中的价值

Thiago J R Rezende1, Emilien Petit2, Young Woo Park3,4,5

  • 1Department of Neurology, School of Medical Sciences, University of Campinas, Campinas, Brazil.

概括

磁共振成像 (MRI) 测量,特别是子体积测量,显示出作为脊髓小脑动症 (SCA) 试验敏感终点的前景. 这些MRI结果可以显著减少预防性和早期干预性研究的样本大小要求.

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