,SCN2A

Jiaxiang Wu1,2, Xiaoling Chen1,2, Jingliang Zhang1,2

  • 1Borch Department of Medicinal Chemistry and Molecular Pharmacology, College of Pharmacy, Purdue University, West Lafayette, IN 47907, USA.

Science advances
|February 18, 2026
PubMed
概括

大脑器官中的人类微质子类型揭示了神经发育和自闭症中的作用. 向微质GABAB受体,通过减少突触修剪,为SCN2A突变相关的自闭症提供了潜在的治疗方法.