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Updated: Jul 14, 2026

High-throughput and Comprehensive Drug Surveillance Using Multisegment Injection-Capillary Electrophoresis-Mass Spectrometry
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Published on: April 23, 2019

对于患有基尿症的青少年的佩格瓦利治疗:一项多站点研究

Suzanne Hollander1,2, Briana Valli1,3, Erika Vucko4

  • 1Division of Genetics and Genomics Boston Children's Hospital Boston Massachusetts USA.

JIMD reports
|February 20, 2026
PubMed
概括

佩格瓦里亚斯在患有基尿症 (PKU) 的青少年中有效降低氨水平,但在过渡学年中,停药率会增加. 早些时候开始这种酶疗法可能会改善长期治疗的成功.

关键词:
坚持性 坚持性青少年 青少年 青少年佩格瓦里亚斯 (Pegvaliase) 是一个氨酸氨酸是一种氨酸.氨氨酸氨基酸酶基尿症 基尿症

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