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Pietro Riguzzi1,2, Emma Grover1, Marianela Schiava1
1Translational and Clinical Research Institute, Newcastle University and Newcastle Hospitals NHS Foundation Trust, John Walton Muscular Dystrophy Research Centre, Newcastle upon Tyne, UK.
贝克尔肌肉发育不良症 (BMD) 的纵向呼吸衰退是渐进的和可变的,行走能力的丧失预示着更快的衰退. 这些发现有助于为BMD患者开发个性化呼吸监测和临床试验策略.
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