规划适应性平台试验的关键考虑:第1部分

Anders Granholm1, Morten Hylander Møller2, Aldana Rosso3

  • 1Department of Intensive Care, Copenhagen University Hospital - Rigshospitalet, Copenhagen, Denmark; Section of Biostatistics, Department of Public Health, University of Copenhagen, Copenhagen, Denmark; Platform Trial Unit, Value and Coherence, Copenhagen University Hospital - Rigshospitalet, Copenhagen, Denmark; Collaboration for Research in Intensive Care (CRIC), Copenhagen, Denmark.

概括

适应性平台试验 (APT) 在临床研究中提供了灵活性和效率,但计划起来很复杂. 本指南为设计这些复杂的随机临床试验的研究人员提供了必要的考虑因素.