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A E Deconinck1, J A Rafael, J A Skinner

  • 1Department of Biochemistry, University of Oxford, United Kingdom.

Cell
|August 22, 1997
PubMed
概括

缺乏双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双双的小鼠表现出杜氏肌肉衰竭 (DMD) 的症状,包括过早死亡. 这种新模型为DMD提供了洞察力,并有助于评估基因治疗策略.