Related Experiment Videos
Cystic fibrosis gene therapy trials and tribulations
1Johns Hopkins Hospital, Baltimore, Maryland 21287, USA. pzeitli@jhmi.edu
Abstract
No abstract available in PubMed .
Related Concept Videos
Articles linked to this work by shared authors, journal, and citation graph.
Therapeutic strategies to correct malfunction of CFTR.
Paediatric respiratory reviews·2003
In utero AAV-mediated gene transfer to rabbit pulmonary epithelium.
Molecular therapy : the journal of the American Society of Gene Therapy·2001
Induction of HSP70 promotes DeltaF508 CFTR trafficking.
American journal of physiology. Lung cellular and molecular physiology·2001
Type I, II, III, IV, and V cystic fibrosis transmembrane conductance regulator defects and opportunities for therapy.
Current opinion in pulmonary medicine·2000
Protein-based masks to unlock conditional activation of therapeutics.
Molecular therapy : the journal of the American Society of Gene Therapy·2026
Optimization of AsCas12f1-Mediated Long-Term Gene Repression.
Molecular therapy : the journal of the American Society of Gene Therapy·2026
Ammonium tetrathiomolybdate improves auditory and vestibular function after gentamicin exposure via the NRF2-GPX4 axis.
Molecular therapy : the journal of the American Society of Gene Therapy·2026
BRD4 Inhibition Mitigates Acute and Chronic Corneal Injury Following Topical Nitrogen Mustard Exposure.
Molecular therapy : the journal of the American Society of Gene Therapy·2026
AAV-mediated CBLN1 replacement rescues hereditary ataxia caused by biallelic CBLN1 variants.
Molecular therapy : the journal of the American Society of Gene Therapy·2026
Inhaled nanosilica orchestrates a pulmonary macrophage-NK cell axis for memory-like NK programming toward synergistic cancer immunotherapy.
Molecular therapy : the journal of the American Society of Gene Therapy·2026
Role of health digital twins in oncology drug development - a primer.
Frontiers in oncology·2026
Research progress and clinical translation prospects of the urinary tract microbiome in prostate cancer.
Frontiers in immunology·2026
Therapeutic regulation of gut microbiota in gastric cancer: mechanisms, strategies, and clinical prospects.
Frontiers in microbiology·2026
Operationalizing patient flow in high-complexity service lines: a health system perspective using oncology care.
Frontiers in health services·2026