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Increased oral bioavailability of paclitaxel by GF120918 in mice through selective modulation of P-glycoprotein

H A Bardelmeijer1, J H Beijnen, K R Brouwer

  • 1Department of Clinical Chemistry, The Netherlands Cancer Institute (Antoni van Leeuwenhoek Huis), Amsterdam.

Insights

GF120918 significantly enhances oral paclitaxel bioavailability in mice by inhibiting P-glycoprotein. This experimental drug offers a promising alternative to cyclosporin A for cancer patients needing improved paclitaxel absorption.

Area of Science:

  • Pharmacology
  • Drug Discovery
  • Cancer Therapeutics

Background:

  • Oral paclitaxel bioavailability is limited by intestinal P-glycoprotein.
  • Cyclosporin A enhances paclitaxel bioavailability but has immunosuppressive side effects.
  • Need for alternative P-glycoprotein inhibitors for cancer therapy.

Purpose of the Study:

  • Evaluate GF120918, a novel P-glycoprotein inhibitor, for enhancing oral paclitaxel bioavailability.
  • Compare GF120918's efficacy in wild-type and mdr1ab knockout mice.
  • Assess GF120918's safety profile regarding paclitaxel metabolism and elimination.

Main Methods:

  • Administered GF120918 orally before paclitaxel dosing in wild-type and mdr1ab knockout mice.
  • Quantified paclitaxel plasma levels using high-performance liquid chromatography.
  • Calculated pharmacokinetic parameters, including area under the concentration-time curve and oral bioavailability.

Main Results:

  • GF120918 increased oral paclitaxel bioavailability by 6.6-fold in wild-type mice (8.5% to 40.2%).
  • GF120918 did not alter paclitaxel pharmacokinetics in mdr1ab knockout mice.
  • Paclitaxel pharmacokinetics in wild-type mice with GF120918 mimicked those in knockout mice, indicating selective intestinal P-glycoprotein inhibition.

Conclusions:

  • GF120918 effectively and selectively inhibits intestinal P-glycoprotein, significantly improving oral paclitaxel bioavailability.
  • GF120918 demonstrates a favorable safety profile, without interfering with paclitaxel metabolism or elimination.
  • GF120918 is a promising candidate for further clinical investigation in cancer patients.

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