The current status of clinical gene therapy

Mass spectrometry of murine leukemia virus core proteins.

Journal of virological methods·2010

Internally calibrated quantification of VEGF in human plasma by fluorescence immunoassays in disposable elastomeric microfluidic devices.

Journal of chromatography. B, Analytical technologies in the biomedical and life sciences·2009

Electrical microfluidic pressure gauge for elastomer microelectromechanical systems.

Journal of applied physics·2009

Experimentally validated quantitative linear model for the device physics of elastomeric microfluidic valves.

Journal of applied physics·2009

Membrane-proximal cytoplasmic domain of Moloney murine leukemia virus envelope tail facilitates fusion.

Experimental and molecular pathology·2008

Membrane activity of an amphiphilic alpha-helical membrane-proximal cytoplasmic domain of the MoMuLV envelope glycoprotein.

Experimental and molecular pathology·2008

Triple-Target CRISPR Strategy to Block HIV Entry and Replication in Permissive Cells.

Human gene therapy·2026

Perivascular Astrocytic Gliosis Induced by Retinal Gene Therapy.

Human gene therapy·2026

Durational Study of Persistent Transduction of Rhesus Macaque Lung and Other Organs Following Single Dosing with AAV1-CFTR.

Human gene therapy·2026

Real-World Data from a Single-Center, Large Academic Centralized Manufacturing of CD19 CAR T Cells in an Industry Partnership.

Human gene therapy·2026

Streamlining Genetically Modified Organism Regulatory Classification in UK Gene Therapy Clinical Trials: A UK Pharmacy Perspective.

Human gene therapy·2026

Physiologically Regulated Frataxin Gene Replacement Restores Neurological Function in a Mouse Model of Friedreich Ataxia.

Human gene therapy·2026

Polycation chain length determines the in vivo mRNA delivery efficiency of block copolymer micelles.

Biomaterials science·2026

Driving Drugs Deeper: Force-Driven Microneedle Systems for Active Therapy and Their Road Towards Clinical Implementation.

Small (Weinheim an der Bergstrasse, Germany)·2026

Mumio Potentiates Temozolomide by Inducing Apoptosis and Ferroptosis in Glioblastoma Cells.

Current pharmaceutical design·2026

Current Targeted Nanoparticle Therapy for Alzheimer's Disease: Current Advances and Future Prospects.

Current neurovascular research·2026

Clinical Presentation, Diagnosis, Treatment, and Outcome of Heart Disease in Becker Muscular Dystrophy.

Anatolian journal of cardiology·2026

Clinical Pharmacology of Eplontersen, the First Approved GalNAc-Conjugated Antisense Oligonucleotide.

Journal of clinical pharmacology·2026

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The current status of clinical gene therapy

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Mass spectrometry of murine leukemia virus core proteins.

Internally calibrated quantification of VEGF in human plasma by fluorescence immunoassays in disposable elastomeric microfluidic devices.

Electrical microfluidic pressure gauge for elastomer microelectromechanical systems.

Experimentally validated quantitative linear model for the device physics of elastomeric microfluidic valves.

Membrane-proximal cytoplasmic domain of Moloney murine leukemia virus envelope tail facilitates fusion.

Membrane activity of an amphiphilic alpha-helical membrane-proximal cytoplasmic domain of the MoMuLV envelope glycoprotein.

Triple-Target CRISPR Strategy to Block HIV Entry and Replication in Permissive Cells.

Perivascular Astrocytic Gliosis Induced by Retinal Gene Therapy.

Durational Study of Persistent Transduction of Rhesus Macaque Lung and Other Organs Following Single Dosing with AAV1-CFTR.

Real-World Data from a Single-Center, Large Academic Centralized Manufacturing of CD19 CAR T Cells in an Industry Partnership.

Streamlining Genetically Modified Organism Regulatory Classification in UK Gene Therapy Clinical Trials: A UK Pharmacy Perspective.

Physiologically Regulated Frataxin Gene Replacement Restores Neurological Function in a Mouse Model of Friedreich Ataxia.

Polycation chain length determines the in vivo mRNA delivery efficiency of block copolymer micelles.

Driving Drugs Deeper: Force-Driven Microneedle Systems for Active Therapy and Their Road Towards Clinical Implementation.

Mumio Potentiates Temozolomide by Inducing Apoptosis and Ferroptosis in Glioblastoma Cells.

Current Targeted Nanoparticle Therapy for Alzheimer's Disease: Current Advances and Future Prospects.

Clinical Presentation, Diagnosis, Treatment, and Outcome of Heart Disease in Becker Muscular Dystrophy.

Clinical Pharmacology of Eplontersen, the First Approved GalNAc-Conjugated Antisense Oligonucleotide.

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