Clinical protocol of human gene transfer for hemophilia B

Implantation of autologous skin fibroblast genetically modified to secrete clotting factor IX partially corrects the hemorrhagic tendencies in two hemophilia B patients.

Chinese medical journal·1996

Retinol (vitamin A) inhibits sister chromatid exchanges and cell cycle delay induced by cyclophosphamide and aflatoxin B1 in Chinese hamster V79 cells.

Carcinogenesis·1982

Effect of tumor promoter 12-O-tetradecanoyl-phorbol 13-acetate on induction of sister-chromatid exchanges in Chinese hamster V79 cells treated with mutagens.

Mutation research·1981

Induction of sister-chromatid exchanges and cell cycle delay in cultured mammalian cells treated with eight organophosphorus pesticides.

Mutation research·1981

Sister chromatid exchanges and chromosome aberrations in V79 cells induced by aflatoxin B1, B2, G1 and G2 with or without metabolic activation.

Carcinogenesis·1980

Engineering Human Hematopoietic Stem and Progenitor Cells for Antigen Expression in Antigen-Presenting Cells.

Human gene therapy·2026

Triple-Target CRISPR Strategy to Block HIV Entry and Replication in Permissive Cells.

Human gene therapy·2026

Perivascular Astrocytic Gliosis Induced by Retinal Gene Therapy.

Human gene therapy·2026

Durational Study of Persistent Transduction of Rhesus Macaque Lung and Other Organs Following Single Dosing with AAV1-CFTR.

Human gene therapy·2026

Real-World Data from a Single-Center, Large Academic Centralized Manufacturing of CD19 CAR T Cells in an Industry Partnership.

Human gene therapy·2026

Streamlining Genetically Modified Organism Regulatory Classification in UK Gene Therapy Clinical Trials: A UK Pharmacy Perspective.

Human gene therapy·2026

Biologic Therapy for Severe Asthma: Biomarker-Guided Precision Treatment and Immunopathological Mechanisms.

Journal of visualized experiments : JoVE·2026

Discovery and development of a bispecific antibody for the treatment of hemophilia.

Proceedings of the National Academy of Sciences of the United States of America·2026

A patient-derived missense mouse model of Kabuki syndrome 1.

Disease models & mechanisms·2026

Residual HIV activity and host immunometabolic remodeling during antiretroviral therapy: implications for cardiovascular-kidney-metabolic risk.

Frontiers in immunology·2026

Correction: Coexisting PTEN and SDHB mutations in a pediatric patient with PTEN hamartoma tumor syndrome: a case report.

Frontiers in pediatrics·2026

Atogepant modulates brain connectivity in episodic migraine: a longitudinal exploratory fMRI study.

Frontiers in neurology·2026

Related Experiment Videos

Clinical protocol of human gene transfer for hemophilia B

Related Concept Videos

Implantation of autologous skin fibroblast genetically modified to secrete clotting factor IX partially corrects the hemorrhagic tendencies in two hemophilia B patients.

Retinol (vitamin A) inhibits sister chromatid exchanges and cell cycle delay induced by cyclophosphamide and aflatoxin B1 in Chinese hamster V79 cells.

Effect of tumor promoter 12-O-tetradecanoyl-phorbol 13-acetate on induction of sister-chromatid exchanges in Chinese hamster V79 cells treated with mutagens.

Induction of sister-chromatid exchanges and cell cycle delay in cultured mammalian cells treated with eight organophosphorus pesticides.

Sister chromatid exchanges and chromosome aberrations in V79 cells induced by aflatoxin B1, B2, G1 and G2 with or without metabolic activation.

Engineering Human Hematopoietic Stem and Progenitor Cells for Antigen Expression in Antigen-Presenting Cells.

Triple-Target CRISPR Strategy to Block HIV Entry and Replication in Permissive Cells.

Perivascular Astrocytic Gliosis Induced by Retinal Gene Therapy.

Durational Study of Persistent Transduction of Rhesus Macaque Lung and Other Organs Following Single Dosing with AAV1-CFTR.

Real-World Data from a Single-Center, Large Academic Centralized Manufacturing of CD19 CAR T Cells in an Industry Partnership.

Streamlining Genetically Modified Organism Regulatory Classification in UK Gene Therapy Clinical Trials: A UK Pharmacy Perspective.

Biologic Therapy for Severe Asthma: Biomarker-Guided Precision Treatment and Immunopathological Mechanisms.

Discovery and development of a bispecific antibody for the treatment of hemophilia.

A patient-derived missense mouse model of Kabuki syndrome 1.

Residual HIV activity and host immunometabolic remodeling during antiretroviral therapy: implications for cardiovascular-kidney-metabolic risk.

Correction: Coexisting PTEN and SDHB mutations in a pediatric patient with PTEN hamartoma tumor syndrome: a case report.

Atogepant modulates brain connectivity in episodic migraine: a longitudinal exploratory fMRI study.

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Clinical protocol of human gene transfer for hemophilia B

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