Related Experiment Video
Updated: Aug 24, 2026
06:51
Systemic Delivery of MicroRNA Using Recombinant Adeno-associated Virus Serotype 9 to Treat Neuromuscular Diseases in Rodents
Published on: August 10, 2018
Toxic RNA in the nucleus: unstable microsatellite expression in neuromuscular disease
Keith R Nykamp1, Maurice S Swanson
1Department of Molecular Genetics and Microbiology, Powell Gene Therapy Center, University of Florida College of Medicine, Gainesville, Florida 32610-0266, USA.
Progress in Molecular and Subcellular Biology
|April 29, 2004
Abstract
No abstract available in PubMed .
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