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Lentiviral Vector-mediated Gene Therapy of Hepatocytes Ex Vivo for Autologous Transplantation in Swine
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Effective gene therapy in an authentic model of Tay-Sachs-related diseases

M Begoña Cachón-González1, Susan Z Wang1, Andrew Lynch2

  • 1*Department of Medicine, University of Cambridge, Level 5, Box 157, Addenbrooke's Hospital, Hills Road, Cambridge CB2 2QQ, United Kingdom.

Proceedings of the National Academy of Sciences of the United States of America
|June 28, 2006
PubMed

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