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Are rare diseases still orphans or happily adopted? The challenges of developing and using orphan medicinal products

James W Dear1, Pajaree Lilitkarntakul, David J Webb

  • 1Clinical Pharmacology Unit, Centre for Cardiovascular Science, University of Edinburgh, Queen's Medical Research Institute, Edinburgh, UK.

British Journal of Clinical Pharmacology
|August 29, 2006
PubMed

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