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Systemic Delivery of MicroRNA Using Recombinant Adeno-associated Virus Serotype 9 to Treat Neuromuscular Diseases in Rodents
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Published on: August 10, 2018

[Gene therapy of ALS with short interfering RNA]

Takanori Yokota1

  • 1Department of Neurology and Neurological Science, Tokyo Medical and Dental University, 1-5-45 Yushima, Bunkyo-ku, Tokyo 113-8519, Japan.

Brain and Nerve = Shinkei Kenkyu No Shinpo
|November 1, 2007
PubMed

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