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Hematopoietic stem cell gene therapy for adenosine deaminase deficient-SCID

Alessandro Aiuti1, Immacolata Brigida, Francesca Ferrua

  • 1San Raffaele Telethon Institute for Gene Therapy (HSR-TIGET) and Pediatric Immunohematology and Bone Marrow Transplant Unit, Scientific Institute HS Raffaele, Via Olgettina 58, 20132, Milan, Italy. a.aiuti@hsr.it

Immunologic Research
|February 19, 2009
PubMed

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