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Systemic Delivery of MicroRNA Using Recombinant Adeno-associated Virus Serotype 9 to Treat Neuromuscular Diseases in Rodents
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[Myotonic dystrophy: therapeutic approaches to RNA toxicity]

Masayuki Nakamori1, Masanori P Takahashi

  • 1Department of Neurology, Osaka University Graduate School of Medicine, Suida, Osaka, Japan.

Brain and Nerve = Shinkei Kenkyu No Shinpo
|November 10, 2011
PubMed

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