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[Toward gene and cell therapy using human artificial chromosome].

Yasuhiro Kazuki1, Mitsuo Oshimura

  • 1Department of Biomedical Science, Institute of Regenerative Medicine and Biofunction, Graduate School of Medical Science, Tottori University.

Nihon Rinsho. Japanese Journal of Clinical Medicine
|January 17, 2012
PubMed
Summary

Human artificial chromosomes (HACs) offer stable gene delivery for physiological regulation. Combining HACs with patient-specific stem cells shows promise for treating genetic diseases like Duchenne muscular dystrophy.

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