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AAV2 gene therapy readministration in three adults with congenital blindness

Jean Bennett1, Manzar Ashtari, Jennifer Wellman

  • 1F. M. Kirby Center for Molecular Ophthalmology, Scheie Eye Institute, University of Pennsylvania, 309 Stellar-Chance Labs, 422 Curie Boulevard, Philadelphia, PA 19104, USA. jebennet@mail.med.upenn.edu

Science Translational Medicine
|February 11, 2012
PubMed

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