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Antisense oligonucleotide therapeutics for inherited neurodegenerative diseases

Amber L Southwell1, Niels H Skotte, C Frank Bennett

  • 1Centre for Molecular Medicine and Therapeutics, Child and Family Research Institute, University of British Columbia, Vancouver, V5Z 4H4, Canada. asouthwell@cmmt.ubc.ca

Trends in Molecular Medicine
|October 3, 2012
PubMed

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