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[Recurrent acidosis with hypoglycemia in an infant: fructose-1,6-diphosphatase deficiency]

P J Fischer1, W Hecker

  • 1Kinderklinik des Olgahospitals, Pädiatrisches Zentrum, Stuttgart.

Klinische Padiatrie
|March 1, 1990
PubMed

Insights

Fructose-1,6-diphosphatase deficiency causes hypoglycemia and lactic acidosis in infants during fasting. Diagnosis via liver biopsy and treatment with dietary changes are crucial for managing this metabolic disorder.

Area of Science:

  • Biochemistry
  • Pediatric Metabolism
  • Enzyme Deficiencies

Background:

  • Fructose-1,6-diphosphatase is a critical enzyme in gluconeogenesis, the pathway for glucose synthesis.
  • Deficiency in this enzyme disrupts glucose homeostasis, particularly during fasting states.

Observation:

  • A seven-month-old infant experienced recurrent episodes of acidosis and hypoglycemia.
  • These episodes were consistently triggered by fasting and febrile infections.

Findings:

  • Diagnosis was confirmed by identifying fructose-1,6-diphosphatase enzyme deficiency in a liver biopsy.
  • This deficiency directly links to the observed metabolic disturbances.

Implications:

  • Early diagnosis and management are vital for preventing severe complications in affected infants.
  • Treatment strategies involve dietary modifications (avoiding fructose/sucrose) and prompt management of acute metabolic crises.

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