How I treat severe combined immunodeficiency

H Bobby Gaspar1, Waseem Qasim, E Graham Davies

  • 1Centre for Immunodeficiency, Molecular Immunology Unit, University College London Institute of Child Health, London, United Kingdom; and.

Blood
|October 12, 2013
PubMed
Summary

Severe combined immunodeficiency (SCID) is a group of genetic disorders affecting lymphocyte development. Advances in hematopoietic stem cell transplantation and gene therapy offer improved survival and tailored treatments for SCID patients.

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