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Electroporation-Based Genetic Modification of Primary Human Pigment Epithelial Cells Using the Sleeping Beauty Transposon System
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Promising and delivering gene therapies for vision loss

Livia S Carvalho1, Luk H Vandenberghe1

  • 1Schepens Eye Research Institute, Massachusetts Eye and Ear Infirmary, Department of Ophthalmology, Harvard Medical School, Harvard University, 20 Staniford Street, Boston, MA 02114, USA.

Vision Research
|August 6, 2014
PubMed

Keywords:
AAVClinical trialGene therapyLCALentiviral vectorRetina

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