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Adherence to tetrahydrobiopterin therapy in patients with phenylketonuria

Frances Rohr1, Ann Wessel1, Matthew Brown1

  • 1Boston Children's Hospital, 300 Longwood Avenue, Boston, MA, USA.

Molecular Genetics and Metabolism
|December 4, 2014
PubMed

Keywords:
AdherenceBH4KuvanPhenylketonuriaSapropterin dihydrochloride

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